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Cystinosis: the past, present and future

Cystinosis: the past, present and future

by Max Verhage | Oct 6, 2025 | Blog

Cystinosis is a rare hereditary disease which leads to accumulation of cystine in the lysosomes causing organ failure. The disease manifests in all organs, but the kidneys and the eyes are affected first. Even though for cystinosis there is a therapy available,...

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